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COST Action BM1207

Networking towards clinical application of antisense-mediated exon skipping Involving all key stakeholders (clinicians, scientists, industry, patients & regulators) Facilitate the clinical development of antisense-mediated exon skipping for rare diseases

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COST Action BM1207

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  1. Networking towards clinical application of antisense-mediated exon skipping Involving all key stakeholders (clinicians, scientists, industry, patients & regulators) • Facilitate the clinical development of antisense-mediated exon skipping for rare diseases • Exploit exon skipping for as many patients as possible Objectives • Achieve consensus biochemical outcome measures • New regulatory models to allow testing of personalized medicine approaches • Foster synergistic work (workshops and key stakeholder meetings and exchange visits) • Address therapeutic misconception by training early stage researchers Current parties involved France, Germany, Israel, Italy, Netherlands, Norway, Spain, Sweden and United Kingdom If you are interested to join, please contact the Chair of this Action Annemieke Aartsma-Rus, a.m.rus@lumc.nl COST Action BM1207

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