Cystinosis Treatment Market Size, Share, Outlook, and Opportunity Analysis, 2018 – 2026.

1. CYSTINOSIS TREATMENT MARKET ANALYSIS INDUSTRY INSIGHTS, TRENDS, OUTLOOK, AND OPPORTUNITY ANALYSIS, 2020–2027 © Coherent market Insights. All Rights Reserved © Coherent market Insights. All Rights Reserved

2. REPORT DESCRIPTION Cystinosis Treatment Market - Overview Cystinosis Treatment Market is a condition characterized by accumulation of the cystine (amino acid) within cells. High amount of cystine damages cells and often forms crystals that can damage tissues and organs. The eyes and kidneys are mainly susceptible to damage; however, the pancreas, muscles, testes, and thyroid can also be affected. Cystinosis is categorized into three different types; nephropathic, non-nephropathic or ocular, and intermediate cystinosis. Nephropathic (infantile) cystinosis is the most severe and common form of cystinosis. Renal Fanconi syndrome and growth failure are usually the first noticeable symptoms of this disorder. Intermediate cystinosis is characterized by symptoms similar to that of nephropathic cystinosis. However, these symptoms are not prominent till age of 8-20 years. All three types of cystinosis occur due to mutations in the CTNS gene. Mutations in CTNS gene cause deficiency of a transporter protein called cystinosin. Cystinosin normally moves cystine out of the lysosomes, which are compartments in the cell that recycle and digest materials. Defects in cystinosin, allows accumulation of cystine and forms crystals in the lysosomes and its buildup damages cells in the eyes and kidneys. According to National Institutes of Health (NIH), cystinosis affects around 1 in 100,000 to 200,000 infants globally. Cystinosis is the most common cause of renal Fanconi syndrome in children and accounts for nearly 5% of all childhood cases of kidney failure. Fanconi syndrome, a rare disorder of kidney tubule function results in excess amounts of potassium, uric acid, glucose, phosphates, bicarbonate, and certain amino acids excreted in the urine. Browse Research Reports: https://www.coherentmarketinsights.com/ongoing- © Coherent market Insights. All Rights Reserved insight/cystinosis-treatment-market-1660

3. REPORT DESCRIPTION Cysteine depleting therapy can significantly reduce cysteine levels inside the cells. It improves growth and decreases kidney damage in children. Symptomatic therapy treats renal Fanconi syndrome with a high intake of electrolytes and fluids to prevent extreme body dehydration. Sodium bicarbonate, potassium, sodium citrate, and magnesium can help to keep standard electrolyte stability. Acetyl cholinesterase (ACE) inhibitors are also used sometimes to limit the growth of the renal disease. Various government grants to support the diagnosis and treatment of cystinosis is boosting growth of the market. For instance, in 2013, the Cystinosis Research Foundation awarded six grants worth US $1.29 million to Cystinosis researchers for developing better treatments and a cure for the disease. Organizations such as Cystinosis Research Network are responsible to spread awareness regarding disease by celebrating Cystinosis Awareness Day on May 7, every year. Furthermore, product approval by the Food and Drug Administration (FDA) is expected to boost growth of the cystinosis treatment market over the forecast period. In 2013, the FDA approved the delayed-release formulation of cysteamine bitartrate (DR-C) for patients aged 6 years and above, and the label was expanded in 2015 to include children age two years. Cysteamine is a cystine-depleting agents that reduces cystine levels in cells. It has proven to be effective in preventing or delaying renal failure and improving growth of children with Cystinosis Request a Sample copy of this reports :https://www.coherentmarketinsights.com/insight/request-sample/1660 © Coherent market Insights. All Rights Reserved

4. REPORT DESCRIPTION Cystinosis treatment Market Regional Insights Regional segmentation of Cystinosis treatment market by Coherent Market Insights, includes North America, Latin America, Europe, Asia Pacific, Middle East, and Africa. North America is the expected to dominate the cystinosis treatment market. According to an article published by Cystinosis Research Network, an estimated 15 new nephropathic cystinosis cases are diagnosed in the U.S. annually. Moreover, the network also works on increasing awareness about disease among regional population. High prevalence rate of cystinosis in Europe is expected to drive growth of the cystinosis treatment market in the region. According to National Institutes of Health (NIH), cystinosis affects 1 in 26,000 persons in France. Cystinosis Treatment Market Competitive Landscape Key players operating in the cystinosis treatment market include Avrobio, Inc., Gilead, Mylan N.V., Novartis AG, and Orizon Pharma Plc. Companies in the cystinosis treatment market are focusing on new product development to gain major revenue share. For instance, Avrobio Inc. is planing to initiate clinical development of two gene therapy candidates for cystinosis and Gaucher disease by mid-2019. Cystinosis Treatment Market Taxonomy Buy-Now this Research Report @ https://www.coherentmarketinsights.com/insight/buy-now/1660 © Coherent market Insights. All Rights Reserved

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6. ABOUT CMI SECTOR COVERAGE BIOTECHNOLOGY CLINICAL DIAGNOSTIC HEALTHCARE IT MEDICAL DEVICES MEDICAL IMAGING PHARMACEUTICAL OUR CLIENTS  Global Leading Equipment and System Manufacturers  Marketing Consultancies and the Advertising Industry  Component Providers and System Integrators  Private and Government organization  Distributors, Retailors and Value Added Resellers  Outsourcing Companies  Healthcare IT Solutions Developers  Universities and Business Schools. © Coherent market Insights. All Rights Reserved

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